Project Team


Known as ‘London’s Global University’, University College London (UCL) employs 4,000 academic and research staff in over 50 departments and institutes… more >

Region Hovedstaden

Region Hovedstaden is a non-academic, non-profit public body with 40,000 full time employees, of which 4,700 are employed in R&D… more >

Centre National de la Recherche Scientifique

CNRS is a government-funded research organization under the administrative authority of French Ministry of Research… more >

Catholic University of the Sacred Heart

The Department of Pediatrics and the Neuromuscular Unit of the Catholic University in Rome have a longstanding experience in the study of cognitive disorders in… more >

Transpharmation Ireland Ltd.

TIL was established in 2014 at Trinity College in Dublin. The company is now a recognized world leader in behavioural and biomarker research applied to… more >

Synthena AG

Synthena AG has been established in 2007 as a development stage biotechnology company aiming to develop and commercialize new life saving oligonucleotide therapeutics for… more >

Consorzio Futuro in Ricerca

CFR is a private non ‐ profit organization originally founded by a number of local organizations in the Ferrara area… more >

University of Newcastle upon Tyne

Newcastle University is one of the top research-intensive universities in the UK. Newcastle University and Newcastle Hospitals NHS Foundation Trust work together towards… more >

University of Versailles Saint Quentin en Yvelines

The laboratory “biothérapies of neuromuscular diseases” is part of a mixed research unit (U1179-UVSQ-Inserm) based at the Faculty of Health Sciences of the… more >

Universidad Complutense de Madrid

UCM is a public research university located in Madrid (Spain), and one of the oldest and largest universities in Europe. The Department of Psychobiology… more >

Great Ormond Street Hospital

Great Ormond Street Hospital for Children NHS Foundation Trust (GOSH) is a national centre of excellence in the provision of specialist children’s health care, currently… more >

Stichting Duchenne Data Foundation

Stitching Duchenne Data Foundation (DDF) is a non-profit patient initiated and managed organization. It is a worldwide collaboration in order to enhance the understanding of… more >

Leiden University Medical Center

LUMC is one of the major medical centres in the Netherlands funded by the Dutch Government. It employs nearly 7000 people… more >

National Center of Neurology and Psychiatry

The National Center of Neurology and Psychiatry (NCNP), affiliated to the Ministry of Health, Labour and Welfare, Japan is composed of… more >


Kempenhaeghe is a specialized expertise center and tertiary clinic for epilepsy, sleep medicine and neurocognition in neurological learning disabilities… more >

Imagine Institute of Genetic Diseases

As the leading European center for research, care and education on genetic diseases, Imagine’s goal is to change the lives of families affected by genetic diseases… more >

World Duchenne Organization

World Duchenne Organization is a worldwide organisation dedicated to finding a cure and viable treatments for DMD, to promoting good standards of care, and to informing parents… more >

Trinity College Dublin

Trinity College was founded by royal charter in 1592 and today has over 18,000 students; 13,087 undergraduates and 4,994 postgraduates. Positioned in the heart of… more >